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Q35105699-F046132A-A30C-4F1B-82B7-57F11DF645D3
Q35105699-F046132A-A30C-4F1B-82B7-57F11DF645D3
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Statement
http://www.wikidata.org/entity/statement/Q35105699-F046132A-A30C-4F1B-82B7-57F11DF645D3
Nonsense suppressor therapies rescue peroxisome lipid metabolism and assembly in cells from patients with specific PEX gene mutations
P2860
Q35105699-F046132A-A30C-4F1B-82B7-57F11DF645D3
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35105699-F046132A-A30C-4F1B-82B7-57F11DF645D3
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wasDerivedFrom
328c58508e19a019c22fa85a26fb49a87b32265f
P2860
Safety, tolerability, and pharmacokinetics of PTC124, a nonaminoglycoside nonsense mutation suppressor, following single- and multiple-dose administration to healthy male and female adult volunteers.