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Q35710895-132EF0CE-8945-4D81-885F-F8884F388FE1
Q35710895-132EF0CE-8945-4D81-885F-F8884F388FE1
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35710895-132EF0CE-8945-4D81-885F-F8884F388FE1
Stable or improved neurological manifestations during miglustat therapy in patients from the international disease registry for Niemann-Pick disease type C: an observational cohort study.
P2860
Q35710895-132EF0CE-8945-4D81-885F-F8884F388FE1
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35710895-132EF0CE-8945-4D81-885F-F8884F388FE1
rank
NormalRank
type
BestRank
Statement
wasDerivedFrom
32c4045e624330e6405ab4c7af5a79e57f80bb6e
P2860
Long-term efficacy of miglustat in paediatric patients with Niemann-Pick disease type C.