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Q35923467-1B7D639F-CD94-4821-8E84-20FA0A9CFC6B
Q35923467-1B7D639F-CD94-4821-8E84-20FA0A9CFC6B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35923467-1B7D639F-CD94-4821-8E84-20FA0A9CFC6B
CNS-directed gene therapy for lysosomal storage diseases
P2860
Q35923467-1B7D639F-CD94-4821-8E84-20FA0A9CFC6B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35923467-1B7D639F-CD94-4821-8E84-20FA0A9CFC6B
rank
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type
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wasDerivedFrom
e0de552c8bcaa84309f5e9d906ebb73ce6cbfdec
P2860
Murine mucopolysaccharidosis type VII: long term therapeutic effects of enzyme replacement and enzyme replacement followed by bone marrow transplantation.