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Q35923476-10733F69-7563-411B-A03C-CD00DFCC6E18
Q35923476-10733F69-7563-411B-A03C-CD00DFCC6E18
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35923476-10733F69-7563-411B-A03C-CD00DFCC6E18
Gene therapy for lysosomal storage diseases (LSDs) in large animal models.
P2860
Q35923476-10733F69-7563-411B-A03C-CD00DFCC6E18
BestRank
Statement
http://www.wikidata.org/entity/statement/Q35923476-10733F69-7563-411B-A03C-CD00DFCC6E18
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9c148e66c6747822af9c7f2d75ef985ef16b1bfd
P2860
Mucopolysaccharidosis I cats mount a cytotoxic T lymphocyte response after neonatal gene therapy that can be blocked with CTLA4-Ig.