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Q36014761-004AED16-76DC-4165-8C20-C3121E1E51DE
Q36014761-004AED16-76DC-4165-8C20-C3121E1E51DE
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http://www.wikidata.org/entity/statement/Q36014761-004AED16-76DC-4165-8C20-C3121E1E51DE
Therapy development for spinal muscular atrophy in SMN independent targets.
P2860
Q36014761-004AED16-76DC-4165-8C20-C3121E1E51DE
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36014761-004AED16-76DC-4165-8C20-C3121E1E51DE
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wasDerivedFrom
f049ac4b16cb57ead87319b2ef58da4203103171
P2860
Disruption of an SF2/ASF-dependent exonic splicing enhancer in SMN2 causes spinal muscular atrophy in the absence of SMN1.