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Q36014761-1BC4928B-41D2-466C-A964-E9C7CB3E9A74
Q36014761-1BC4928B-41D2-466C-A964-E9C7CB3E9A74
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36014761-1BC4928B-41D2-466C-A964-E9C7CB3E9A74
Therapy development for spinal muscular atrophy in SMN independent targets.
P2860
Q36014761-1BC4928B-41D2-466C-A964-E9C7CB3E9A74
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36014761-1BC4928B-41D2-466C-A964-E9C7CB3E9A74
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wasDerivedFrom
f049ac4b16cb57ead87319b2ef58da4203103171
P2860
Delivery of bifunctional RNAs that target an intronic repressor and increase SMN levels in an animal model of spinal muscular atrophy.