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Q36014761-24D0EF2D-3416-48E4-A943-6B9D5B98E679
Q36014761-24D0EF2D-3416-48E4-A943-6B9D5B98E679
BestRank
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http://www.wikidata.org/entity/statement/Q36014761-24D0EF2D-3416-48E4-A943-6B9D5B98E679
Therapy development for spinal muscular atrophy in SMN independent targets.
P2860
Q36014761-24D0EF2D-3416-48E4-A943-6B9D5B98E679
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36014761-24D0EF2D-3416-48E4-A943-6B9D5B98E679
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wasDerivedFrom
f049ac4b16cb57ead87319b2ef58da4203103171
P2860
LBH589 induces up to 10-fold SMN protein levels by several independent mechanisms and is effective even in cells from SMA patients non-responsive to valproate