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Q36014761-37C301D6-8B98-484B-9764-CC9CF6E97CE4
Q36014761-37C301D6-8B98-484B-9764-CC9CF6E97CE4
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http://www.wikidata.org/entity/statement/Q36014761-37C301D6-8B98-484B-9764-CC9CF6E97CE4
Therapy development for spinal muscular atrophy in SMN independent targets.
P2860
Q36014761-37C301D6-8B98-484B-9764-CC9CF6E97CE4
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36014761-37C301D6-8B98-484B-9764-CC9CF6E97CE4
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f049ac4b16cb57ead87319b2ef58da4203103171
P2860
A single administration of morpholino antisense oligomer rescues spinal muscular atrophy in mouse