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Q36014761-4C07F3E6-E7C9-420B-B25D-A189E0CCF348
Q36014761-4C07F3E6-E7C9-420B-B25D-A189E0CCF348
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http://www.wikidata.org/entity/statement/Q36014761-4C07F3E6-E7C9-420B-B25D-A189E0CCF348
Therapy development for spinal muscular atrophy in SMN independent targets.
P2860
Q36014761-4C07F3E6-E7C9-420B-B25D-A189E0CCF348
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36014761-4C07F3E6-E7C9-420B-B25D-A189E0CCF348
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f049ac4b16cb57ead87319b2ef58da4203103171
P2860
Delivery of a read-through inducing compound, TC007, lessens the severity of a spinal muscular atrophy animal model.