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Q36286233-45ACE9F8-D9A5-4F9F-9C92-80CCED14D4C3
Q36286233-45ACE9F8-D9A5-4F9F-9C92-80CCED14D4C3
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http://www.wikidata.org/entity/statement/Q36286233-45ACE9F8-D9A5-4F9F-9C92-80CCED14D4C3
Revised Hammersmith Scale for spinal muscular atrophy: A SMA specific clinical outcome assessment tool.
P2860
Q36286233-45ACE9F8-D9A5-4F9F-9C92-80CCED14D4C3
BestRank
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http://www.wikidata.org/entity/statement/Q36286233-45ACE9F8-D9A5-4F9F-9C92-80CCED14D4C3
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9c782bff6b66ea3f5eab0a603cb63ccabc2572e6
P2860
Results from a phase 1 study of nusinersen (ISIS-SMN(Rx)) in children with spinal muscular atrophy.