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Q36322222-32F8B297-28B2-4857-91D2-5B0358CFA852
Q36322222-32F8B297-28B2-4857-91D2-5B0358CFA852
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Statement
http://www.wikidata.org/entity/statement/Q36322222-32F8B297-28B2-4857-91D2-5B0358CFA852
Mechanistic principles of antisense targets for the treatment of spinal muscular atrophy
P2860
Q36322222-32F8B297-28B2-4857-91D2-5B0358CFA852
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36322222-32F8B297-28B2-4857-91D2-5B0358CFA852
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266f442e6dc9884743625cc66a13b72938f1f2bd
P2860
Spinal muscular atrophy associated with progressive myoclonic epilepsy is caused by mutations in ASAH1