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Q36521756-C0DBEB07-14AE-4F89-9179-DA91D16D549B
Q36521756-C0DBEB07-14AE-4F89-9179-DA91D16D549B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36521756-C0DBEB07-14AE-4F89-9179-DA91D16D549B
A GLP-Compliant Toxicology and Biodistribution Study: Systemic Delivery of an rAAV9 Vector for the Treatment of Mucopolysaccharidosis IIIB.
P2860
Q36521756-C0DBEB07-14AE-4F89-9179-DA91D16D549B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36521756-C0DBEB07-14AE-4F89-9179-DA91D16D549B
rank
NormalRank
type
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Statement
wasDerivedFrom
1edca3bf877422b19ca0d1eae89468b2afaa06e0
P2860
AAV-mediated gene delivery in adult GM1-gangliosidosis mice corrects lysosomal storage in CNS and improves survival