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Q36572002-FA935274-EE6F-40FA-9B5A-C7D232D2112E
Q36572002-FA935274-EE6F-40FA-9B5A-C7D232D2112E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36572002-FA935274-EE6F-40FA-9B5A-C7D232D2112E
Disease and patient characteristics in NP-C patients: findings from an international disease registry.
P2860
Q36572002-FA935274-EE6F-40FA-9B5A-C7D232D2112E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36572002-FA935274-EE6F-40FA-9B5A-C7D232D2112E
rank
NormalRank
type
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Statement
wasDerivedFrom
7a410a4e8657ee0cffa451908e7b81b60315b2f3
P2860
Long-term efficacy of miglustat in paediatric patients with Niemann-Pick disease type C.