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Q36879362-5F3A2072-2831-4C03-8148-37680DCE70E9
Q36879362-5F3A2072-2831-4C03-8148-37680DCE70E9
BestRank
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http://www.wikidata.org/entity/statement/Q36879362-5F3A2072-2831-4C03-8148-37680DCE70E9
Normalisation of brain spectroscopy findings in Niemann-Pick disease type C patients treated with miglustat.
P2860
Q36879362-5F3A2072-2831-4C03-8148-37680DCE70E9
BestRank
Statement
http://www.wikidata.org/entity/statement/Q36879362-5F3A2072-2831-4C03-8148-37680DCE70E9
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wasDerivedFrom
d9dd6f2872045c464721833be3c4fb8304575048
P2860
Miglustat in adult and juvenile patients with Niemann-Pick disease type C: long-term data from a clinical trial.