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Q38097869-3F579F31-10C8-4914-B2E4-F1077F0580E6
Q38097869-3F579F31-10C8-4914-B2E4-F1077F0580E6
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http://www.wikidata.org/entity/statement/Q38097869-3F579F31-10C8-4914-B2E4-F1077F0580E6
Glucocerebrosidase inhibitors for the treatment of Gaucher disease.
P2860
Q38097869-3F579F31-10C8-4914-B2E4-F1077F0580E6
BestRank
Statement
http://www.wikidata.org/entity/statement/Q38097869-3F579F31-10C8-4914-B2E4-F1077F0580E6
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wasDerivedFrom
e6fabf7607b9e0d7ad822957dab5838ceeb95a3a
P2860
The pharmacological chaperone AT2220 increases recombinant human acid α-glucosidase uptake and glycogen reduction in a mouse model of Pompe disease.