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Q39340546-60049691-4E23-42CC-8BBE-CA1063AA9292
Q39340546-60049691-4E23-42CC-8BBE-CA1063AA9292
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39340546-60049691-4E23-42CC-8BBE-CA1063AA9292
Therapeutic approaches for spinal muscular atrophy (SMA).
P2860
Q39340546-60049691-4E23-42CC-8BBE-CA1063AA9292
BestRank
Statement
http://www.wikidata.org/entity/statement/Q39340546-60049691-4E23-42CC-8BBE-CA1063AA9292
rank
NormalRank
type
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Statement
wasDerivedFrom
7f0681fda45b27119dc0bf27d43b0948fd15690e
P2860
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study.