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Q40319080-DE0EAFC9-5545-4F00-BC0F-0795496552C9
Q40319080-DE0EAFC9-5545-4F00-BC0F-0795496552C9
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40319080-DE0EAFC9-5545-4F00-BC0F-0795496552C9
Novel Biomarkers of Human GM1 Gangliosidosis Reflect the Clinical Efficacy of Gene Therapy in a Feline Model.
P2860
Q40319080-DE0EAFC9-5545-4F00-BC0F-0795496552C9
BestRank
Statement
http://www.wikidata.org/entity/statement/Q40319080-DE0EAFC9-5545-4F00-BC0F-0795496552C9
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wasDerivedFrom
7e3c9519e70918d25ec1b3fefa80e4d0fb8f5ddb
P2860
AAV-mediated gene delivery in adult GM1-gangliosidosis mice corrects lysosomal storage in CNS and improves survival