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Q41671504-4AD8E838-39D7-4F92-B039-FE56F2EE2473
Q41671504-4AD8E838-39D7-4F92-B039-FE56F2EE2473
BestRank
Statement
http://www.wikidata.org/entity/statement/Q41671504-4AD8E838-39D7-4F92-B039-FE56F2EE2473
Double-target Antisense U1snRNAs Correct Mis-splicing Due to c.639+861C>T and c.639+919G>A GLA Deep Intronic Mutations.
P2860
Q41671504-4AD8E838-39D7-4F92-B039-FE56F2EE2473
BestRank
Statement
http://www.wikidata.org/entity/statement/Q41671504-4AD8E838-39D7-4F92-B039-FE56F2EE2473
rank
NormalRank
type
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Statement
wasDerivedFrom
2d9d3829cb84dd5c59a352b431e76a2a4540d708
P2860
Natural course of Fabry disease and the effectiveness of enzyme replacement therapy: a systematic review and meta-analysis: effectiveness of ERT in different disease stages.