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Q45869556-0A3696F5-AF78-42BC-9234-11E69C690D67
Q45869556-0A3696F5-AF78-42BC-9234-11E69C690D67
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45869556-0A3696F5-AF78-42BC-9234-11E69C690D67
U1 snRNA-mediated gene therapeutic correction of splice defects caused by an exceptionally mild BBS mutation.
P2860
Q45869556-0A3696F5-AF78-42BC-9234-11E69C690D67
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45869556-0A3696F5-AF78-42BC-9234-11E69C690D67
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wasDerivedFrom
aa8212bdd3d0202fc87347d9418ce69fbda1c8b6
P2860
B-cell-specific transgene expression using a self-inactivating retroviral vector with human CD19 promoter and viral post-transcriptional regulatory element.