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Q45877711-F5BFD3FD-4E7A-4130-988B-3C5253D93657
Q45877711-F5BFD3FD-4E7A-4130-988B-3C5253D93657
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Statement
http://www.wikidata.org/entity/statement/Q45877711-F5BFD3FD-4E7A-4130-988B-3C5253D93657
Improved efficacy of gene therapy approaches for Pompe disease using a new, immune-deficient GSD-II mouse model.
P2860
Q45877711-F5BFD3FD-4E7A-4130-988B-3C5253D93657
BestRank
Statement
http://www.wikidata.org/entity/statement/Q45877711-F5BFD3FD-4E7A-4130-988B-3C5253D93657
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wasDerivedFrom
32f1e73834002d1fb4e2683b9081a4461e970c3b
P2860
Conditional tissue-specific expression of the acid alpha-glucosidase (GAA) gene in the GAA knockout mice: implications for therapy