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Q46849509-CD07A439-0A17-416D-9124-06D663F640B0
Q46849509-CD07A439-0A17-416D-9124-06D663F640B0
BestRank
Statement
http://www.wikidata.org/entity/statement/Q46849509-CD07A439-0A17-416D-9124-06D663F640B0
Pseudoexon exclusion by antisense therapy in 6-pyruvoyl-tetrahydropterin synthase deficiency.
P2860
Q46849509-CD07A439-0A17-416D-9124-06D663F640B0
BestRank
Statement
http://www.wikidata.org/entity/statement/Q46849509-CD07A439-0A17-416D-9124-06D663F640B0
rank
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type
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Statement
wasDerivedFrom
bc61b114412b3e4c920f70b2aa5557b0844aec20
P2860
In vivo correction of a Menkes disease model using antisense oligonucleotides.