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Q47301525-342604AD-731E-4F2E-B0CF-3D7C616FB175
Q47301525-342604AD-731E-4F2E-B0CF-3D7C616FB175
BestRank
Statement
http://www.wikidata.org/entity/statement/Q47301525-342604AD-731E-4F2E-B0CF-3D7C616FB175
Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase.
P2860
Q47301525-342604AD-731E-4F2E-B0CF-3D7C616FB175
BestRank
Statement
http://www.wikidata.org/entity/statement/Q47301525-342604AD-731E-4F2E-B0CF-3D7C616FB175
rank
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wasDerivedFrom
6b4f60b8ba1cf285db85fc24643ef4ff69c3e686
P2860
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in classic-infantile patients with Pompe disease