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1
Q47547335-EB2F0FA2-5C7E-4CA4-BEC2-F7111363656A
Q47547335-EB2F0FA2-5C7E-4CA4-BEC2-F7111363656A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q47547335-EB2F0FA2-5C7E-4CA4-BEC2-F7111363656A
Pre-clinical Safety and Off-Target Studies to Support Translation of AAV-Mediated RNAi Therapy for FSHD.
P2860
Q47547335-EB2F0FA2-5C7E-4CA4-BEC2-F7111363656A
BestRank
Statement
http://www.wikidata.org/entity/statement/Q47547335-EB2F0FA2-5C7E-4CA4-BEC2-F7111363656A
rank
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type
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wasDerivedFrom
71d28d6c5d543226d45e7a75dcb655ab08f6b43d
P2860
PABPN1 gene therapy for oculopharyngeal muscular dystrophy