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Q47558790-FB15528E-884B-4AF8-8C79-9F2E342FA024
Q47558790-FB15528E-884B-4AF8-8C79-9F2E342FA024
BestRank
Statement
http://www.wikidata.org/entity/statement/Q47558790-FB15528E-884B-4AF8-8C79-9F2E342FA024
Gene therapy for Mucopolysaccharidoses.
P2860
Q47558790-FB15528E-884B-4AF8-8C79-9F2E342FA024
BestRank
Statement
http://www.wikidata.org/entity/statement/Q47558790-FB15528E-884B-4AF8-8C79-9F2E342FA024
rank
NormalRank
type
BestRank
Statement
wasDerivedFrom
1aa13ab1a39359bddda026757fb04b4ba9638c40
P2860
Efficient CNS targeting in adult mice by intrathecal infusion of single-stranded AAV9-GFP for gene therapy of neurological disorders.