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Q50056656-1F2F607C-3493-4651-99DB-5BF32F82C45C
Q50056656-1F2F607C-3493-4651-99DB-5BF32F82C45C
BestRank
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http://www.wikidata.org/entity/statement/Q50056656-1F2F607C-3493-4651-99DB-5BF32F82C45C
Long-Term Improvement of Neurological Signs and Metabolic Dysfunction in a Mouse Model of Krabbe's Disease after Global Gene Therapy.
P2860
Q50056656-1F2F607C-3493-4651-99DB-5BF32F82C45C
BestRank
Statement
http://www.wikidata.org/entity/statement/Q50056656-1F2F607C-3493-4651-99DB-5BF32F82C45C
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623187188afa62f36070f137f9beb6c4ae4eda3d
P2860
Bone marrow transplantation augments the effect of brain- and spinal cord-directed adeno-associated virus 2/5 gene therapy by altering inflammation in the murine model of globoid-cell leukodystrophy.