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Q50200829-CD6A2DB4-4CA9-4247-9CFC-CA37D946DAC8
Q50200829-CD6A2DB4-4CA9-4247-9CFC-CA37D946DAC8
BestRank
Statement
http://www.wikidata.org/entity/statement/Q50200829-CD6A2DB4-4CA9-4247-9CFC-CA37D946DAC8
Nusinersen for the treatment of spinal muscular atrophy.
P2860
Q50200829-CD6A2DB4-4CA9-4247-9CFC-CA37D946DAC8
BestRank
Statement
http://www.wikidata.org/entity/statement/Q50200829-CD6A2DB4-4CA9-4247-9CFC-CA37D946DAC8
rank
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wasDerivedFrom
8dbb58476355f4f0121b3f40bb7ba9b6488c66a2
P2860
Splice-switching antisense oligonucleotides as therapeutic drugs