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Q51025979-BEC8A950-EA00-40B2-BCE5-692968446A10
Q51025979-BEC8A950-EA00-40B2-BCE5-692968446A10
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http://www.wikidata.org/entity/statement/Q51025979-BEC8A950-EA00-40B2-BCE5-692968446A10
A-44G transition in SMN2 intron 6 protects patients with spinal muscular atrophy.
P2860
Q51025979-BEC8A950-EA00-40B2-BCE5-692968446A10
BestRank
Statement
http://www.wikidata.org/entity/statement/Q51025979-BEC8A950-EA00-40B2-BCE5-692968446A10
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af56bcfb44c79130a81522af58189986f65b74ea
P2860
Targeting SR proteins improves SMN expression in spinal muscular atrophy cells.