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1
Q53099264-FCDCA171-ADF2-4D3F-9A4D-B699B6638192
Q53099264-FCDCA171-ADF2-4D3F-9A4D-B699B6638192
BestRank
Statement
http://www.wikidata.org/entity/statement/Q53099264-FCDCA171-ADF2-4D3F-9A4D-B699B6638192
Mucopolysaccharidosis type I and craniosynostosis.
P2860
Q53099264-FCDCA171-ADF2-4D3F-9A4D-B699B6638192
BestRank
Statement
http://www.wikidata.org/entity/statement/Q53099264-FCDCA171-ADF2-4D3F-9A4D-B699B6638192
rank
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type
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Statement
wasDerivedFrom
49b25f1229e9700d7a66dce440341ec88ab5c455
P2860
Minicircle DNA-based gene therapy coupled with immune modulation permits long-term expression of α-L-iduronidase in mice with mucopolysaccharidosis type I