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Q58763192-65AC3D0E-43A3-4795-910C-DE07DAB461AA
Q58763192-65AC3D0E-43A3-4795-910C-DE07DAB461AA
BestRank
Statement
http://www.wikidata.org/entity/statement/Q58763192-65AC3D0E-43A3-4795-910C-DE07DAB461AA
Rare disease registries: potential applications towards impact on development of new drug treatments
P2860
Q58763192-65AC3D0E-43A3-4795-910C-DE07DAB461AA
BestRank
Statement
http://www.wikidata.org/entity/statement/Q58763192-65AC3D0E-43A3-4795-910C-DE07DAB461AA
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b4ab803fae7c9350ef88a36993ec3145dca8a323
P2860
Clinical outcomes after long-term treatment with alglucosidase alfa in infants and children with advanced Pompe disease.