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Q58763192-7DAED81D-C0E1-404E-AB33-4D64AA27F22E
Q58763192-7DAED81D-C0E1-404E-AB33-4D64AA27F22E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q58763192-7DAED81D-C0E1-404E-AB33-4D64AA27F22E
Rare disease registries: potential applications towards impact on development of new drug treatments
P2860
Q58763192-7DAED81D-C0E1-404E-AB33-4D64AA27F22E
BestRank
Statement
http://www.wikidata.org/entity/statement/Q58763192-7DAED81D-C0E1-404E-AB33-4D64AA27F22E
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b4ab803fae7c9350ef88a36993ec3145dca8a323
P2860
Limitations of drug registries to evaluate orphan medicinal products for the treatment of lysosomal storage disorders.