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161026e153f7b93a896f38075aef68a4f7712eab
161026e153f7b93a896f38075aef68a4f7712eab
Reference
http://www.wikidata.org/reference/161026e153f7b93a896f38075aef68a4f7712eab
Q25105466-df6f3c3a-46ea-86bb-8f36-5d6bbbae4581
wasDerivedFrom
161026e153f7b93a896f38075aef68a4f7712eab
Reference
http://www.wikidata.org/reference/161026e153f7b93a896f38075aef68a4f7712eab
type
Reference
P248
Treatment of infantile-onset spinal muscular atrophy with nusinersen: a phase 2, open-label, dose-escalation study.