Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in classic-infantile patients with Pompe disease
about
The quality of economic evaluations of ultra-orphan drugs in Europe - a systematic reviewInduced pluripotent stem cell models of lysosomal storage disorders.State of rare disease management in Southeast Asia.Showing Value in Newborn Screening: Challenges in Quantifying the Effectiveness and Cost-Effectiveness of Early Detection of Phenylketonuria and Cystic Fibrosis.Economic Evaluations of Pharmaceuticals Granted a Marketing Authorisation Without the Results of Randomised Trials: A Systematic Review and Taxonomy.What is known about the cost-effectiveness of orphan drugs? Evidence from cost-utility analyses.Rescue of Pompe disease in mice by AAV-mediated liver delivery of secretable acid α-glucosidase.Cardiac response to enzyme replacement therapy in infantile Pompe disease with severe hypertrophic cardiomyopathy.Intracranial arterial abnormalities in patients with late onset Pompe disease (LOPD).
P2860
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P2860
Cost-effectiveness of enzyme replacement therapy with alglucosidase alfa in classic-infantile patients with Pompe disease
description
2014 nî lūn-bûn
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2014 թուականի Մայիսին հրատարակուած գիտական յօդուած
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2014 թվականի մայիսին հրատարակված գիտական հոդված
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2014年の論文
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年学术文章
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2014年學術文章
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name
Cost-effectiveness of enzyme r ...... le patients with Pompe disease
@ast
Cost-effectiveness of enzyme r ...... le patients with Pompe disease
@en
type
label
Cost-effectiveness of enzyme r ...... le patients with Pompe disease
@ast
Cost-effectiveness of enzyme r ...... le patients with Pompe disease
@en
prefLabel
Cost-effectiveness of enzyme r ...... le patients with Pompe disease
@ast
Cost-effectiveness of enzyme r ...... le patients with Pompe disease
@en
P2093
P2860
P356
P1476
Cost-effectiveness of enzyme r ...... le patients with Pompe disease
@en
P2093
Ans T van der Ploeg
Iris Hoogenboom-Plug
Leona Hakkaart
Maureen P M H Rutten-Van Mölken
W Ken Redekop
P2860
P2888
P356
10.1186/1750-1172-9-75
P577
2014-05-16T00:00:00Z
P5875
P6179
1052140771