Gene suppression strategies for dominantly inherited neurodegenerative diseases: lessons from Huntington's disease and spinocerebellar ataxia.
about
Reduction of Huntington's Disease RNA Foci by CAG Repeat-Targeting Reagents.Haplotype-based stratification of Huntington's disease.Post-modern therapeutic approaches for progressive myoclonus epilepsy.ASPsiRNA: A Resource of ASP-siRNAs Having Therapeutic Potential for Human Genetic Disorders and Algorithm for Prediction of Their Inhibitory Efficacy.Gene suppression approaches to neurodegeneration.Optimization of trans-Splicing for Huntington's Disease RNA Therapy.Novel allele-specific quantification methods reveal no effects of adult onset CAG repeats on HTT mRNA and protein levels.Therapies targeting DNA and RNA in Huntington's disease.Protein Misfolding and Aggregation as a Therapeutic Target for Polyglutamine Diseases.Polyglutamine spinocerebellar ataxias - from genes to potential treatments.Permanent inactivation of Huntington's disease mutation by personalized allele-specific CRISPR/Cas9.Precise Excision of the CAG Tract from the Huntingtin Gene by Cas9 Nickases.Translation of MicroRNA-Based Huntingtin-Lowering Therapies from Preclinical Studies to the Clinic.Population-specific genetic modification of Huntington's disease in Venezuela.Metformin reverses early cortical network dysfunction and behavior changes in Huntington's disease
P2860
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P2860
Gene suppression strategies for dominantly inherited neurodegenerative diseases: lessons from Huntington's disease and spinocerebellar ataxia.
description
2015 nî lūn-bûn
@nan
2015 թուականի Հոկտեմբերին հրատարակուած գիտական յօդուած
@hyw
2015 թվականի հոտեմբերին հրատարակված գիտական հոդված
@hy
2015年の論文
@ja
2015年論文
@yue
2015年論文
@zh-hant
2015年論文
@zh-hk
2015年論文
@zh-mo
2015年論文
@zh-tw
2015年论文
@wuu
name
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@ast
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@en
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@nl
type
label
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@ast
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@en
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@nl
prefLabel
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@ast
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@en
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@nl
P2093
P2860
P356
P1476
Gene suppression strategies fo ...... se and spinocerebellar ataxia.
@en
P2093
Holly B Kordasiewicz
Jodi L McBride
Megan S Keiser
P2860
P304
P356
10.1093/HMG/DDV442
P577
2015-10-26T00:00:00Z