Retroviral-mediated transfer of genomic globin genes leads to regulated production of RNA and protein.
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Hematopoietic stem cell gene therapy:assessing the relevance of preclinical modelsHigh-level beta-globin expression after retroviral transfer of locus activation region-containing human beta-globin gene derivatives into murine erythroleukemia cells.Expression of the human beta-globin gene following retroviral-mediated transfer into multipotential hematopoietic progenitors of mice.Gene therapy for hemoglobinopathies: the state of the field and the future.Correction of glucocerebrosidase deficiency after retroviral-mediated gene transfer into hematopoietic progenitor cells from patients with Gaucher disease.Production of human glucocerebrosidase in mice after retroviral gene transfer into multipotential hematopoietic progenitor cells.Effect of human beta (s)-globin chains on cellular properties of red cells from beta-thalassemic mice.An Erythroid-Specific Chromatin Opening Element Increases β-Globin Gene Expression from Integrated Retroviral Gene Transfer Vectors.Globin gene transfer for the treatment of severe hemoglobinopathies: a paradigm for stem cell-based gene therapy.Recombinant adeno-associated virus (rAAV)-mediated expression of a human gamma-globin gene in human progenitor-derived erythroid cells.Adeno-associated virus type 2-mediated transduction of murine hematopoietic cells with long-term repopulating ability and sustained expression of a human globin gene in vivo.Packaging of intron-containing genes into retrovirus vectors by alphavirus vectors.Expression of the neutrophil elastase gene during human bone marrow cell differentiationGene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene.Expression of the human beta-globin gene after retroviral transfer into murine erythroleukemia cells and human BFU-E cells.Design of retrovirus vectors for transfer and expression of the human beta-globin gene.A 36-base-pair core sequence of locus control region enhances retrovirally transferred human beta-globin gene expression.Gene therapy for β-thalassaemia: the continuing challenge.Gene therapy in thalassemia and hemoglobinopathies.Gene therapy: current status and future directions.Recent advances in gene therapy for thalassemia.Development of gene therapy for thalassemia.Gene transfer. A potential approach to gene therapy for sickle cell disease.Slow and Steady Wins The Race? Progress in the Development of Vectors for Gene Therapy of β-Thalassemia and Sickle Cell Disease.Split-intron retroviral vectors: enhanced expression with improved safety.Retroviral vectors produced in the cytoplasmic vaccinia virus system transduce intron-containing genes.Analysis of enhancer function of the HS-40 core sequence of the human alpha-globin cluster.Novel retroviral vector transferring a suicide gene and a selectable marker gene with enhanced gene expression by using a tetracycline-responsive expression system.A lentiviral vector bearing a reverse intron demonstrates superior expression of both proteins and microRNAs.Retroviral vectors for the beta-globin gene that demonstrate improved titer and expression.An in vitro system for efficiently evaluating gene therapy approaches to hemoglobinopathies.Gene Addition Strategies for β-Thalassemia and Sickle Cell Anemia.
P2860
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P2860
Retroviral-mediated transfer of genomic globin genes leads to regulated production of RNA and protein.
description
1987 nî lūn-bûn
@nan
1987 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
1987 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
1987年の論文
@ja
1987年論文
@yue
1987年論文
@zh-hant
1987年論文
@zh-hk
1987年論文
@zh-mo
1987年論文
@zh-tw
1987年论文
@wuu
name
Retroviral-mediated transfer o ...... production of RNA and protein.
@ast
Retroviral-mediated transfer o ...... production of RNA and protein.
@en
Retroviral-mediated transfer o ...... production of RNA and protein.
@nl
type
label
Retroviral-mediated transfer o ...... production of RNA and protein.
@ast
Retroviral-mediated transfer o ...... production of RNA and protein.
@en
Retroviral-mediated transfer o ...... production of RNA and protein.
@nl
prefLabel
Retroviral-mediated transfer o ...... production of RNA and protein.
@ast
Retroviral-mediated transfer o ...... production of RNA and protein.
@en
Retroviral-mediated transfer o ...... production of RNA and protein.
@nl
P2093
P2860
P356
P1476
Retroviral-mediated transfer o ...... production of RNA and protein.
@en
P2093
Karlsson S
Nienhuis AW
Papayannopoulou T
Schweiger SG
Stamatoyannopoulos G
P2860
P304
P356
10.1073/PNAS.84.8.2411
P407
P577
1987-04-01T00:00:00Z