The AAV vector toolkit: poised at the clinical crossroads
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Biology of adeno-associated viral vectors in the central nervous systemMicroRNAs in glioblastoma multiforme pathogenesis and therapeuticsGenome-editing Technologies for Gene and Cell TherapyIon channel remodeling in vascular smooth muscle during hypertension: Implications for novel therapeutic approachesAdeno-associated virus-mediated microRNA delivery and therapeuticsAdeno-associated virus at 50: a golden anniversary of discovery, research, and gene therapy success--a personal perspectiveGene delivery to adipose tissue using transcriptionally targeted rAAV8 vectorsElectron microscopy analysis of a disaccharide analog complex reveals receptor interactions of adeno-associated virusThe structure of AAVrh32.33, a novel gene delivery vectorA lncRNA Perspective into (Re)Building the HeartCurrent understanding of molecular pathology and treatment of cardiomyopathy in duchenne muscular dystrophyGene transfer of mutant mouse cholinesterase provides high lifetime expression and reduced cocaine responses with no evident toxicityCell-penetrating peptide-mediated delivery of TALEN proteins via bioconjugation for genome engineeringBarriers to inhaled gene therapy of obstructive lung diseases: A reviewGene therapy for metachromatic leukodystrophy.Passive immunization against HIV/AIDS by antibody gene transfer.A single intravenous rAAV injection as late as P20 achieves efficacious and sustained CNS Gene therapy in Canavan mice.Virally mediated optogenetic excitation and inhibition of pain in freely moving nontransgenic mice.Overcoming the cystic fibrosis sputum barrier to leading adeno-associated virus gene therapy vectorsSustained AAV-mediated overexpression of CRF in the central amygdala diminishes the depressive-like state associated with nicotine withdrawalQuantification of AAV particle titers by infrared fluorescence scanning of coomassie-stained sodium dodecyl sulfate-polyacrylamide gels.A capillary electrophoresis sequencing method for the identification of mutations in the inverted terminal repeats of adeno-associated virusInfluence of immune responses in gene/stem cell therapies for muscular dystrophies.Gene therapy: charting a future course--summary of a National Institutes of Health Workshop, April 12, 2013.CRISPR/Cas9-mediated genome editing via postnatal administration of AAV vector cures haemophilia B mice.[EXPRESS] Primary sensory neuron-specific interference of TRPV1 signaling by AAV-encoded TRPV1 peptide aptamer attenuates neuropathic pain.Gene transfer to the CNS using recombinant adeno-associated virusSMN-inducing compounds for the treatment of spinal muscular atrophy.Gene therapy for inherited muscle diseases: where genetics meets rehabilitation medicine.Adeno-associated virus (AAV) vectors in gene therapy: immune challenges and strategies to circumvent them.Chondroitin Sulfate is the Primary Receptor for a Peptide-Modified AAV That Targets Brain Vascular Endothelium In Vivo.Modeling Pulmonary Disease Pathways Using Recombinant Adeno-Associated Virus 6.2.Adipose tissue insulin receptor knockdown via a new primate-derived hybrid recombinant AAV serotype.Synthetic virology: engineering viruses for gene deliveryOptimization of the capsid of recombinant adeno-associated virus 2 (AAV2) vectors: the final threshold?Intraganglionic AAV6 results in efficient and long-term gene transfer to peripheral sensory nervous system in adult rats.Capsid serotype and timing of injection determines AAV transduction in the neonatal mice brain.Insight into the mechanism of inhibition of adeno-associated virus by the Mre11/Rad50/Nbs1 complexMultiple roles for sialylated glycans in determining the cardiopulmonary tropism of adeno-associated virus 4Characterization of naturally-occurring humoral immunity to AAV in sheep.
P2860
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P2860
The AAV vector toolkit: poised at the clinical crossroads
description
2012 nî lūn-bûn
@nan
2012年の論文
@ja
2012年論文
@yue
2012年論文
@zh-hant
2012年論文
@zh-hk
2012年論文
@zh-mo
2012年論文
@zh-tw
2012年论文
@wuu
2012年论文
@zh
2012年论文
@zh-cn
name
The AAV vector toolkit: poised at the clinical crossroads
@ast
The AAV vector toolkit: poised at the clinical crossroads
@en
type
label
The AAV vector toolkit: poised at the clinical crossroads
@ast
The AAV vector toolkit: poised at the clinical crossroads
@en
prefLabel
The AAV vector toolkit: poised at the clinical crossroads
@ast
The AAV vector toolkit: poised at the clinical crossroads
@en
P2860
P356
P1433
P1476
The AAV vector toolkit: poised at the clinical crossroads
@en
P2093
Aravind Asokan
R Jude Samulski
P2860
P304
P356
10.1038/MT.2011.287
P577
2012-01-24T00:00:00Z