AAV9-mediated central nervous system-targeted gene delivery via cisterna magna route in mice.
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Ganglionic GFAP + glial Gq-GPCR signaling enhances heart functions in vivoA Single Vector Platform for High-Level Gene Transduction of Central Neurons: Adeno-Associated Virus Vector Equipped with the Tet-Off System.Viral delivery of C9orf72 hexanucleotide repeat expansions in mice leads to repeat-length-dependent neuropathology and behavioural deficits.Efficient CNS targeting in adult mice by intrathecal infusion of single-stranded AAV9-GFP for gene therapy of neurological disorders.Disease correction by AAV-mediated gene therapy in a new mouse model of mucopolysaccharidosis type IIID.Intracranial AAV-IFN-β gene therapy eliminates invasive xenograft glioblastoma and improves survival in orthotopic syngeneic murine model.Plastin 3 Promotes Motor Neuron Axonal Growth and Extends Survival in a Mouse Model of Spinal Muscular Atrophy.Translating SOD1 Gene Silencing toward the Clinic: A Highly Efficacious, Off-Target-free, and Biomarker-Supported Strategy for fALS.
P2860
Q30354373-D1677E50-791E-4BBB-9110-1A6730B58471Q36242844-DA67C4C1-E955-4711-95E9-0BE4BDFB26DDQ38760731-79A969FA-F16F-4045-BF0E-4961BE8C2A26Q40235080-C8742F6F-E1BA-437E-ACDB-9532CAADF651Q40277701-F131FF44-F5E4-4697-B3CC-AF02DF81ACF0Q40375925-C4F65BA8-92D8-4182-A5BD-6A827CCCB814Q54253770-7D6FDDFD-3E09-4960-AB5E-CD3FE5E1A778Q55399094-3D2C2464-788E-4BD7-B20B-E410F6CF8555
P2860
AAV9-mediated central nervous system-targeted gene delivery via cisterna magna route in mice.
description
2016 nî lūn-bûn
@nan
2016年の論文
@ja
2016年論文
@yue
2016年論文
@zh-hant
2016年論文
@zh-hk
2016年論文
@zh-mo
2016年論文
@zh-tw
2016年论文
@wuu
2016年论文
@zh
2016年论文
@zh-cn
name
AAV9-mediated central nervous ...... cisterna magna route in mice.
@ast
AAV9-mediated central nervous ...... cisterna magna route in mice.
@en
type
label
AAV9-mediated central nervous ...... cisterna magna route in mice.
@ast
AAV9-mediated central nervous ...... cisterna magna route in mice.
@en
prefLabel
AAV9-mediated central nervous ...... cisterna magna route in mice.
@ast
AAV9-mediated central nervous ...... cisterna magna route in mice.
@en
P2860
P50
P356
P1476
AAV9-mediated central nervous ...... cisterna magna route in mice.
@en
P2093
Ian Coldicott
Vera Lukashchuk
P2860
P356
10.1038/MTM.2015.55
P577
2016-02-17T00:00:00Z