Efficient whole-body transduction with trans-splicing adeno-associated viral vectors - sprookjes - yvandenbroek - TriplyDB

Efficient whole-body transduction with trans-splicing adeno-associated viral vectors

Efficient whole-body transduction with trans-splicing adeno-associated viral vectors

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Homologous recombination mediates functional recovery of dysferlin deficiency following AAV5 gene transfer Advances in gene therapy for muscular dystrophies Gene therapy in the cornea: 2005--present.Ectopic catalase expression in mitochondria by adeno-associated virus enhances exercise performance in mice.Systemic Trans-splicing adeno-associated viral delivery efficiently transduces the heart of adult mdx mouse, a model for duchenne muscular dystrophy The potential of adeno-associated viral vectors for gene delivery to muscle tissue.A NEW RECOMBINANT ADENO-ASSOCIATED VIRUS (AAV)-BASED RANDOM PEPTIDE DISPLAY LIBRARY SYSTEM: INFECTION-DEFECTIVE AAV1.9-3 AS A NOVEL DETARGETED PLATFORM FOR VECTOR EVOLUTION.Adeno-associated virus serotype-9 microdystrophin gene therapy ameliorates electrocardiographic abnormalities in mdx mice.Adeno-associated virus serotype 6 capsid tyrosine-to-phenylalanine mutations improve gene transfer to skeletal muscle.Gene therapy of mdx mice with large truncated dystrophins generated by recombination using rAAV6.Efficient transgene reconstitution with hybrid dual AAV vectors carrying the minimized bridging sequences Gene replacement therapies for duchenne muscular dystrophy using adeno-associated viral vectors.The use of mitochondria-targeted endonucleases to manipulate mtDNA Duchenne muscular dystrophy gene therapy: Lost in translation?Whole body skeletal muscle transduction in neonatal dogs with AAV-9.A potential role of distinctively delayed blood clearance of recombinant adeno-associated virus serotype 9 in robust cardiac transduction.SERCA2a gene transfer improves electrocardiographic performance in aged mdx mice Developmental stage determines efficiency of gene transfer to muscle satellite cells by in utero delivery of adeno-associated virus vector serotype 2/9 AAV.Dysferlin Overlap Vectors Restore Function in Dysferlinopathy Animal Models The evolution of heart gene delivery vectors Humoral immunity to AAV-6, 8, and 9 in normal and dystrophic dogs In vivo gene transfer strategies to achieve partial correction of von Willebrand disease.Manipulation of mtDNA heteroplasmy in all striated muscles of newborn mice by AAV9-mediated delivery of a mitochondria-targeted restriction endonuclease.Frequency and spectrum of genomic integration of recombinant adeno-associated virus serotype 8 vector in neonatal mouse liver Dystrophins carrying spectrin-like repeats 16 and 17 anchor nNOS to the sarcolemma and enhance exercise performance in a mouse model of muscular dystrophy.Dual AAV therapy ameliorates exercise-induced muscle injury and functional ischemia in murine models of Duchenne muscular dystrophy Molecular-targeted therapy for Duchenne muscular dystrophy: progress and potential.Gene doping: the hype and the reality.A single intravenous injection of adeno-associated virus serotype-9 leads to whole body skeletal muscle transduction in dogs.Viral vectors: from virology to transgene expression Adeno-associated virus serotype-9 efficiently transduces the retinal outer plexiform layer Designing heart performance by gene transfer.Recombinant adeno-associated virus serotype 9 in a mouse model of atherosclerosis: Determination of the optimal expression time in vivo.Immune Responses to AAV-Vectors, the Glybera Example from Bench to Bedside.Dual AAV gene therapy for Duchenne muscular dystrophy with a 7-kb mini-dystrophin gene in the canine model.Systemic Delivery of Dysferlin Overlap Vectors Provides Long-Term Gene Expression and Functional Improvement for Dysferlinopathy.B-type natriuretic peptide overexpression ameliorates hepatorenal fibrocystic disease in a rat model of polycystic kidney disease.Systemic delivery of adeno-associated viral vectors.Nanotherapy for Duchenne muscular dystrophy.Functional cystic fibrosis transmembrane conductance regulator expression in cystic fibrosis airway epithelial cells by AAV6.2-mediated segmental trans-splicing

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P2860

Efficient whole-body transduction with trans-splicing adeno-associated viral vectors

http://www.wikidata.org/entity/Q36968872

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2007 nî lūn-bûn

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2007年の論文

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2007年論文

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2007年論文

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2007年論文

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2007年論文

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2007年论文

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2007年论文

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2007年论文

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name

Efficient whole-body transduction with trans-splicing adeno-associated viral vectors

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Efficient whole-body transduction with trans-splicing adeno-associated viral vectors

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prefLabel

Efficient whole-body transduction with trans-splicing adeno-associated viral vectors

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Molecular Therapy

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Efficient whole-body transduction with trans-splicing adeno-associated viral vectors

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Brian Bostick

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Chun Long

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Yongping Yue

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P2860

Novel adeno-associated viruses from rhesus monkeys as vectors for human gene therapy

Method for multiplex cellular detection of mRNAs using quantum dot fluorescent in situ hybridization.

rAAV6-microdystrophin preserves muscle function and extends lifespan in severely dystrophic mice.

Amelioration of laminin-alpha2-deficient congenital muscular dystrophy by somatic gene transfer of miniagrin.

Clades of Adeno-associated viruses are widely disseminated in human tissues.

Systemic delivery of genes to striated muscles using adeno-associated viral vectors.

Endosomal processing limits gene transfer to polarized airway epithelia by adeno-associated virus.

Body-wide gene therapy of Duchenne muscular dystrophy in the mdx mouse model.

Adeno-associated virus serotype 9 vectors transduce murine alveolar and nasal epithelia and can be readministered.

Adeno-associated viruses undergo substantial evolution in primates during natural infections.

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750-755

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scholarly article

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10.1038/SJ.MT.6300081

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4

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15

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Arkasubhra Ghosh

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2007-01-30T00:00:00Z

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6539387

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2581720

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