In vivo delivery of human acid ceramidase via cord blood transplantation and direct injection of lentivirus as novel treatment approaches for Farber disease.
about
Autologous transplantation of lentivector/acid ceramidase-transduced hematopoietic cells in nonhuman primates.Lentivector transduction improves outcomes over transplantation of human HSCs alone in NOD/SCID/Fabry mice.Acid ceramidase treatment enhances the outcome of autologous chondrocyte implantation in a rat osteochondral defect model.Systemic ceramide accumulation leads to severe and varied pathological consequences.Novel application of lentiviral vectors towards treatment of graft-versus-host disease.Odontoid infiltration and spinal compression in Farber Disease: reversal by haematopoietic stem cell transplantation.A cross-sectional quantitative analysis of the natural history of Farber disease: an ultra-orphan condition with rheumatologic and neurological cardinal disease features.Deletion of MCP-1 Impedes Pathogenesis of Acid Ceramidase Deficiency.
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P2860
In vivo delivery of human acid ceramidase via cord blood transplantation and direct injection of lentivirus as novel treatment approaches for Farber disease.
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article científic
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article scientifique
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articolo scientifico
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artigo científico
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bilimsel makale
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scientific article published on 20 September 2008
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vedecký článok
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vetenskaplig artikel
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videnskabelig artikel
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vědecký článek
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name
In vivo delivery of human acid ...... approaches for Farber disease.
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In vivo delivery of human acid ...... approaches for Farber disease.
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type
label
In vivo delivery of human acid ...... approaches for Farber disease.
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In vivo delivery of human acid ...... approaches for Farber disease.
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In vivo delivery of human acid ...... approaches for Farber disease.
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In vivo delivery of human acid ...... approaches for Farber disease.
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P2093
P2860
P1476
In vivo delivery of human acid ...... approaches for Farber disease.
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P2093
Carmen Bedia Girbés
Jeffrey A Medin
Shobha Ramsubir
Stéphane Carpentier
Takahiro Nonaka
Thierry Levade
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P304
P356
10.1016/J.YMGME.2008.08.003
P577
2008-09-20T00:00:00Z