RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice.
about
Gene therapy: charting a future course--summary of a National Institutes of Health Workshop, April 12, 2013.Prospect of gene therapy for cardiomyopathy in hereditary muscular dystrophy.Recombinant adeno-associated virus vectors in the treatment of rare diseases.Fetal stem cells and skeletal muscle regeneration: a therapeutic approach.Genome engineering: a new approach to gene therapy for neuromuscular disorders.Pre-clinical Safety and Off-Target Studies to Support Translation of AAV-Mediated RNAi Therapy for FSHD.
P2860
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice.
description
2014 nî lūn-bûn
@nan
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
2014年论文
@zh
2014年论文
@zh-cn
name
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice.
@en
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice.
@nl
type
label
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice.
@en
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice.
@nl
prefLabel
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice.
@en
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice.
@nl
P2093
P2860
P356
P1476
RNAi-mediated Gene Silencing of Mutant Myotilin Improves Myopathy in LGMD1A Mice
@en
P2093
Carol S Davis
Chady H Hakim
Darcée D Sloboda
Jerry R Mendell
Lindsay M Wallace
Michael A Hauser
Sara E Garwick-Coppens
Scott Q Harper
P2860
P356
10.1038/MTNA.2014.13
P50
P577
2014-04-29T00:00:00Z