Gene therapy using a liver-targeted AAV vector restores nucleoside and nucleotide homeostasis in a murine model of MNGIE.

Gene therapy using a liver-targeted AAV vector restores nucleoside and nucleotide homeostasis in a murine model of MNGIE.

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http://www.wikidata.org/entity/Q39413079
Mitochondrial diseases caused by toxic compound accumulation: from etiopathology to therapeutic approachesToward a therapy for mitochondrial diseaseLiver as a source for thymidine phosphorylase replacement in mitochondrial neurogastrointestinal encephalomyopathyLong term expression of Drosophila melanogaster nucleoside kinase in thymidine kinase 2-deficient mice with no lethal effects caused by nucleotide pool imbalances.Mitochondrial Diseases Part III: Therapeutic interventions in mouse models of OXPHOS deficiencies.Emerging therapies for mitochondrial disorders.Mitochondrial diseases: advances and issues.Mutations causing mitochondrial disease: What is new and what challenges remain?Mitochondrial Neurogastrointestinal Encephalomyopathy Caused by Thymidine Phosphorylase Enzyme Deficiency: From Pathogenesis to Emerging Therapeutic Options.Sustained AMPK activation improves muscle function in a mitochondrial myopathy mouse model by promoting muscle fiber regeneration.Long-Term Restoration of Thymidine Phosphorylase Function and Nucleoside Homeostasis Using Hematopoietic Gene Therapy in a Murine Model of Mitochondrial Neurogastrointestinal Encephalomyopathy.Liver transplant in ethylmalonic encephalopathy: a new treatment for an otherwise fatal disease.Thymidine phosphorylase: A potential new target for treating cardiovascular disease.NEWS and VIEWS: mitochondrial encephalomyopathies.Preclinical Efficacy and Safety Evaluation of Hematopoietic Stem Cell Gene Therapy in a Mouse Model of MNGIE.
P2860

Gene therapy using a liver-targeted AAV vector restores nucleoside and nucleotide homeostasis in a murine model of MNGIE.

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http://www.wikidata.org/entity/Q39413079
description
2014 nî lūn-bûn
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2014年の論文
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2014年論文
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2014年論文
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2014年論文
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2014年論文
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2014年論文
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2014年论文
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2014年论文
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2014年论文
@zh-cn
name
Gene therapy using a liver-tar ...... is in a murine model of MNGIE.
@en
Gene therapy using a liver-tar ...... is in a murine model of MNGIE.
@nl
type
label
Gene therapy using a liver-tar ...... is in a murine model of MNGIE.
@en
Gene therapy using a liver-tar ...... is in a murine model of MNGIE.
@nl
prefLabel
Gene therapy using a liver-tar ...... is in a murine model of MNGIE.
@en
Gene therapy using a liver-tar ...... is in a murine model of MNGIE.
@nl
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Gene therapy using a liver-tar ...... sis in a murine model of MNGIE
@en
P2093
P2860
P304
P31
P356
P433
P478
P50
P577
P5875
P698
P921
P932