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Q33996884-0B818EB8-1CAA-4EE5-9C4D-BD85F696F891
Q33996884-0B818EB8-1CAA-4EE5-9C4D-BD85F696F891
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http://www.wikidata.org/entity/statement/Q33996884-0B818EB8-1CAA-4EE5-9C4D-BD85F696F891
RNAi-based gene therapy for dominant Limb Girdle Muscular Dystrophies.
P2860
Q33996884-0B818EB8-1CAA-4EE5-9C4D-BD85F696F891
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33996884-0B818EB8-1CAA-4EE5-9C4D-BD85F696F891
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b3825c437edf3b70b78ecc7b4b43379bc1b40f8a
P2860
Gene therapy for muscular dystrophy: lessons learned and path forward