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Q33996884-5EDE23E8-476F-4B65-BE62-4D2DE06FFE5B
Q33996884-5EDE23E8-476F-4B65-BE62-4D2DE06FFE5B
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http://www.wikidata.org/entity/statement/Q33996884-5EDE23E8-476F-4B65-BE62-4D2DE06FFE5B
RNAi-based gene therapy for dominant Limb Girdle Muscular Dystrophies.
P2860
Q33996884-5EDE23E8-476F-4B65-BE62-4D2DE06FFE5B
BestRank
Statement
http://www.wikidata.org/entity/statement/Q33996884-5EDE23E8-476F-4B65-BE62-4D2DE06FFE5B
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wasDerivedFrom
b3825c437edf3b70b78ecc7b4b43379bc1b40f8a
P2860
Mutations in myotilin cause myofibrillar myopathy