An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A
about
Management of Charcot-Marie-Tooth disease: improving long-term care with a multidisciplinary approachThe genetics of Charcot-Marie-Tooth disease: current trends and future implications for diagnosis and managementA brief review of recent Charcot-Marie-Tooth research and prioritiesDevelopment of Improved HDAC6 Inhibitors as Pharmacological Therapy for Axonal Charcot-Marie-Tooth DiseasePolytherapy with a combination of three repurposed drugs (PXT3003) down-regulates Pmp22 over-expression and improves myelination, axonal and functional parameters in models of CMT1A neuropathy.A Rasch Analysis of the Charcot-Marie-Tooth Neuropathy Score (CMTNS) in a Cohort of Charcot-Marie-Tooth Type 1A PatientsCombination of acamprosate and baclofen as a promising therapeutic approach for Parkinson's disease.Drug combination therapy increases successful drug repositioning.Validation of differential GDAP1 DNA methylation in alcohol dependence and its potential function as a biomarker for disease severity and therapy outcomeTherapeutic options in Charcot-Marie-Tooth diseases.Charcot-Marie-Tooth 1A: A narrative review with clinical and anatomical perspectives.Promoting peripheral myelin repair.Recent advances in the genetic neuropathies.A meta-analysis of randomized double-blind clinical trials in CMT1A to assess the change from baseline in CMTNS and ONLS scales after one year of treatment.Erratum to: An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1APharmacology and drug development in rare diseases: the attractiveness and expertise of the French medical pharmacology.Treating pediatric neuromuscular disorders: The future is now.Traduction française de l'échelle Charcot-Marie-Tooth Disease Pediatric Scale.
P2860
Q26768401-9155C87A-60FB-41AA-85E6-7D6D69BD9F2EQ26777319-10ED187B-6AF5-454C-9788-29CD01492326Q27012700-AED062A6-DA13-43ED-9EE5-8861712EC377Q33586017-29E35A55-7155-4C6B-937D-332E5806BD30Q34788066-BA345B1A-BA0D-4BFC-B8D4-6A2130DAC13CQ36251291-CD72D002-7A49-4F9A-89F2-BF79B34A4E46Q36254618-8BD5D773-0553-4045-AEC1-BDF9F3666C4AQ37004251-242383A7-EAF8-4A52-9C95-57A9A94DD571Q37082648-C16CE849-1D11-4985-A065-A340EDC7C4CFQ38363677-BB8A728F-E30F-423A-A6C1-E1C86D075CD4Q38604756-D715B9B0-F09F-4648-B862-64FB66CF7064Q38808666-0D5A7B4F-0EA7-4107-B0C8-E9CA2F85A54BQ38943757-C6820BAC-490C-430C-A71C-23BA4D512A44Q42399924-800C2331-FF1A-4236-B697-A0CCFBD38949Q42428283-4A4361CA-1734-4504-AB6F-F7DF0FD8EB81Q47304122-9DC31AB7-E95D-4E0A-8C8D-742E4E47DA9BQ52756417-58653CE7-A164-4C8F-8584-25ACCF8FAA08Q53108544-2AA32688-088F-44E6-98BD-B5B939D97E3D
P2860
An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A
description
2014 nî lūn-bûn
@nan
2014 թուականին հրատարակուած գիտական յօդուած
@hyw
2014 թվականին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@ast
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@en
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@en-gb
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@nl
type
label
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@ast
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@en
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@en-gb
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@nl
prefLabel
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@ast
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@en
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@en-gb
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@nl
P2093
P2860
P50
P3181
P1476
An exploratory randomised doub ...... ot-Marie-Tooth disease type 1A
@en
P2093
Armelle Magot
Arnaud Lacour
Aude Milet
Benoît Funalot
Catherine Scart-Grès
Ilya Chumakov
Jean Pouget
Jean-Michel Vallat
Jonas Mandel
Joëlle Micallef
P2860
P2888
P3181
P356
10.1186/S13023-014-0199-0
P407
P577
2014-01-01T00:00:00Z
P5875
P6179
1052539891