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Q22000603-ECC2A7E7-E051-4F65-A844-DE56C02D919F
Q22000603-ECC2A7E7-E051-4F65-A844-DE56C02D919F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q22000603-ECC2A7E7-E051-4F65-A844-DE56C02D919F
An exploratory randomised double-blind and placebo-controlled phase 2 study of a combination of baclofen, naltrexone and sorbitol (PXT3003) in patients with Charcot-Marie-Tooth disease type 1A
P1433
Q22000603-ECC2A7E7-E051-4F65-A844-DE56C02D919F
BestRank
Statement
http://www.wikidata.org/entity/statement/Q22000603-ECC2A7E7-E051-4F65-A844-DE56C02D919F
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type
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P1433
Orphanet Journal of Rare Diseases