Burden of disease in patients with Morquio A syndrome: results from an international patient-reported outcomes survey.
about
Health-related quality of life in mucopolysaccharidosis: looking beyond biomedical issuesPain assessment using the adolescent pediatric pain tool: a systematic reviewClinical outcomes in a subpopulation of adults with Morquio A syndrome: results from a long-term extension study of elosulfase alfa.Overcoming the barriers to diagnosis of Morquio A syndromePsychological health in adults with morquio syndrome.Atypical presentation of mucopolysaccharidosis type IVARare diseases: matching wheelchair users with rare metabolic, neuromuscular or neurological disorders to electric powered indoor/outdoor wheelchairs (EPIOCs)Parents' experiences of living with, and caring for children, adolescents and young adults with Mucopolysaccharidosis (MPS).Elosulfase Alfa: a review of its use in patients with mucopolysaccharidosis type IVA (Morquio A syndrome).Emerging drugs for the treatment of mucopolysaccharidoses.Lysosomal storage disorders: A review of the musculoskeletal features.Minimal clinically important difference for the 6-min walk test: literature review and application to Morquio A syndrome.Social/economic costs and health-related quality of life of mucopolysaccharidosis patients and their caregivers in Europe.Quality of life in mucopolysaccharidoses: construction of a specific measure using the focus group technique.Voice alterations in patients with Morquio A syndrome.Patient reported outcome measures in rare diseases: a narrative review.International guidelines for the management and treatment of Morquio A syndrome.Safety and physiological effects of two different doses of elosulfase alfa in patients with morquio a syndrome: A randomized, double-blind, pilot study.Impact of elosulfase alfa in patients with morquio A syndrome who have limited ambulation: An open-label, phase 2 study.
P2860
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P2860
Burden of disease in patients with Morquio A syndrome: results from an international patient-reported outcomes survey.
description
2014 nî lūn-bûn
@nan
2014 թուականի Մարտին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի մարտին հրատարակված գիտական հոդված
@hy
2014年の論文
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2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
Burden of disease in patients ...... ient-reported outcomes survey.
@ast
Burden of disease in patients ...... ient-reported outcomes survey.
@en
type
label
Burden of disease in patients ...... ient-reported outcomes survey.
@ast
Burden of disease in patients ...... ient-reported outcomes survey.
@en
prefLabel
Burden of disease in patients ...... ient-reported outcomes survey.
@ast
Burden of disease in patients ...... ient-reported outcomes survey.
@en
P2093
P2860
P356
P1476
Burden of disease in patients ...... ient-reported outcomes survey.
@en
P2093
Christina Lampe
Christine Lavery
Mahmut Coker
Mohit Jain
Sema Kalkan Ucar
P2860
P2888
P356
10.1186/1750-1172-9-32
P577
2014-03-07T00:00:00Z
P5875
P6179
1047563589