Important role of translational science in rare disease innovation, discovery, and drug development.
about
Design, set-up and utility of the UK facioscapulohumeral muscular dystrophy patient registryTranslational Pharmacokinetic/Pharmacodynamic Analysis of MYO-029 Antibody for Muscular Dystrophy.Translating rare-disease therapies into improved care for patients and families: what are the right outcomes, designs, and engagement approaches in health-systems research?Nutritional interventions in primary mitochondrial disorders: Developing an evidence base.Enabling Anyone to Translate Clinically Relevant Ideas to Therapies.Challenges and Hurdles to Business as Usual in Drug Development for Treatment of Rare Diseases.Rare Diseases: Joining Mainstream Research and Treatment Based on Reliable Epidemiological Data.Deficiency of aminopeptidase P1 causes behavioral hyperactivity, cognitive deficits, and hippocampal neurodegeneration.Impact of biobanks on research outcomes in rare diseases: a systematic reviewChallenges in Advanced Therapy Medicinal Product Development: A Survey among Companies in Europe
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P2860
Important role of translational science in rare disease innovation, discovery, and drug development.
description
2014 nî lūn-bûn
@nan
2014 թուականի Օգոստոսին հրատարակուած գիտական յօդուած
@hyw
2014 թվականի օգոստոսին հրատարակված գիտական հոդված
@hy
2014年の論文
@ja
2014年論文
@yue
2014年論文
@zh-hant
2014年論文
@zh-hk
2014年論文
@zh-mo
2014年論文
@zh-tw
2014年论文
@wuu
name
Important role of translationa ...... scovery, and drug development.
@ast
Important role of translationa ...... scovery, and drug development.
@en
Important role of translationa ...... scovery, and drug development.
@nl
type
label
Important role of translationa ...... scovery, and drug development.
@ast
Important role of translationa ...... scovery, and drug development.
@en
Important role of translationa ...... scovery, and drug development.
@nl
prefLabel
Important role of translationa ...... scovery, and drug development.
@ast
Important role of translationa ...... scovery, and drug development.
@en
Important role of translationa ...... scovery, and drug development.
@nl
P2860
P1476
Important role of translationa ...... scovery, and drug development.
@en
P2093
Anne R Pariser
William A Gahl
P2860
P2888
P304
P356
10.1007/S11606-014-2881-2
P478
29 Suppl 3
P577
2014-08-01T00:00:00Z
P5875
P6179
1005222529