Brain-directed gene therapy for lysosomal storage disease: going well beyond the blood- brain barrier.

Brain-directed gene therapy for lysosomal storage disease: going well beyond the blood- brain barrier.

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http://www.wikidata.org/entity/Q34026516
Organelle targeting: third level of drug targetingMolecular simulations of carbohydrates and protein-carbohydrate interactions: motivation, issues and prospectsDeletion of macrophage-inflammatory protein 1 alpha retards neurodegeneration in Sandhoff disease miceBiosynthetic processing of cathepsins and lysosomal degradation are abolished in asparaginyl endopeptidase-deficient miceDisruption of adaptive energy metabolism and elevated ribosomal p-S6K1 levels contribute to INCL pathogenesis: partial rescue by resveratrolGene therapy for the nervous system: challenges and new strategies.Evaluation of neurodegeneration in a mouse model of infantile batten disease by magnetic resonance imaging and magnetic resonance spectroscopy.Nanoparticle transport across the blood brain barrier.Endocytic mechanisms for targeted drug deliveryStructural glycobiology: a game of snakes and ladders.Enhanced efficacy of an AAV vector encoding chimeric, highly secreted acid alpha-glucosidase in glycogen storage disease type II.Neural stem cell transplantation as a therapeutic approach for treating lysosomal storage diseases.An overview of nanosomes delivery mechanisms: trafficking, orders, barriers and cellular effects.Mannitol-facilitated CNS entry of rAAV2 vector significantly delayed the neurological disease progression in MPS IIIB mice.Adeno-associated virus vector-mediated transduction in the cat brain.
P2860

Brain-directed gene therapy for lysosomal storage disease: going well beyond the blood- brain barrier.

Item
http://www.wikidata.org/entity/Q34026516
description
2002 nî lūn-bûn
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2002 թուականի Ապրիլին հրատարակուած գիտական յօդուած
@hyw
2002 թվականի ապրիլին հրատարակված գիտական հոդված
@hy
2002年の論文
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2002年論文
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2002年論文
@zh-hant
2002年論文
@zh-hk
2002年論文
@zh-mo
2002年論文
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2002年论文
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name
Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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type
label
Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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P1433
P1476
P2093
P2860
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P577
P5875
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Brain-directed gene therapy fo ...... yond the blood- brain barrier.
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P2093
P2860
P304
P31
P356
P407
P433
P478
P577
P5875
P698
P921
P932