Lessons learned from the development of enzyme therapy for Gaucher disease.

Lessons learned from the development of enzyme therapy for Gaucher disease.

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http://www.wikidata.org/entity/Q34471677
Brain-directed gene therapy for lysosomal storage disease: going well beyond the blood- brain barrier.The role of microglia in human disease: therapeutic tool or target?Enzyme replacement therapy in newborn mucopolysaccharidosis IVA mice: early treatment rescues bone lesions?Biochemistry of glycosphingolipid storage disorders: implications for therapeutic interventionNovel candidate disease for gene therapy: metachromatic leukodystrophy.Enhancement of drug delivery to bone: characterization of human tissue-nonspecific alkaline phosphatase tagged with an acidic oligopeptide.A review of treatment of Pompe disease in infantsGlucocerebroside: an evolutionary advantage for patients with Gaucher disease and a new immunomodulatory agent.Generation of a Chinese hamster ovary cell line producing recombinant human glucocerebrosidase.Gene therapy for lysosomal storage disorders: recent advances for metachromatic leukodystrophy and mucopolysaccaridosis I.Gaucher disease in Syrian children: common mutations identification, and clinical futures.Viral-mediated delivery of the late-infantile neuronal ceroid lipofuscinosis gene, TPP-I to the mouse central nervous system.
P2860

Lessons learned from the development of enzyme therapy for Gaucher disease.

Item
http://www.wikidata.org/entity/Q34471677
description
2001 nî lūn-bûn
@nan
2001 թուականի Յունուարին հրատարակուած գիտական յօդուած
@hyw
2001 թվականի հունվարին հրատարակված գիտական հոդված
@hy
2001年の論文
@ja
2001年論文
@yue
2001年論文
@zh-hant
2001年論文
@zh-hk
2001年論文
@zh-mo
2001年論文
@zh-tw
2001年论文
@wuu
name
Lessons learned from the development of enzyme therapy for Gaucher disease.
@ast
Lessons learned from the development of enzyme therapy for Gaucher disease.
@en
Lessons learned from the development of enzyme therapy for Gaucher disease.
@nl
type
label
Lessons learned from the development of enzyme therapy for Gaucher disease.
@ast
Lessons learned from the development of enzyme therapy for Gaucher disease.
@en
Lessons learned from the development of enzyme therapy for Gaucher disease.
@nl
prefLabel
Lessons learned from the development of enzyme therapy for Gaucher disease.
@ast
Lessons learned from the development of enzyme therapy for Gaucher disease.
@en
Lessons learned from the development of enzyme therapy for Gaucher disease.
@nl
P1433
P1476
P2093
P2888
P304
P31
P356
P478
P577
P6179
P698
P356
P1433
P1476
Lessons learned from the development of enzyme therapy for Gaucher disease.
@en
P2093
P2888
P304
P31
P356
P478
P577
P6179
P698