Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy. - Wikidata - awgldk - TriplyDB

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy.

Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy.

http://www.wikidata.org/entity/Q35011497

about

Gene therapy in Parkinson's disease: rationale and current status The role of ELOVL1 in very long-chain fatty acid homeostasis and X-linked adrenoleukodystrophy A new generation of human artificial chromosomes for functional genomics and gene therapy Drug delivery trends in clinical trials and translational medicine: challenges and opportunities in the delivery of nucleic acid-based therapeutics Current and future pharmacological treatment strategies in X-linked adrenoleukodystrophy Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemia A transposon and transposase system for human application Lentiviral vector gene therapy: effective and safe?Clinical development of gene therapy: results and lessons from recent successes Production of lentiviral vectors Current and future alternative therapies for beta-thalassemia major Gene Therapy in Cardiac Surgery: Clinical Trials, Challenges, and Perspectives Gene therapy: progress and predictions Peroxisomes in brain development and function Advanced cell therapies: targeting, tracking and actuation of cells with magnetic particles Cell-based therapy technology classifications and translational challenges Bone Marrow Gene Therapy for HIV/AIDS Developments in the treatment of hemophilia B: focus on emerging gene therapy State-of-the-art human gene therapy: part I. Gene delivery technologies Differential diagnosis of Mendelian and mitochondrial disorders in patients with suspected multiple sclerosis The genetic landscape of X-linked adrenoleukodystrophy: inheritance, mutations, modifier genes, and diagnosis A short perspective on gene therapy: Clinical experience on gene therapy of gliomablastoma multiforme Perinatal systemic gene delivery using adeno-associated viral vectors Hematopoietic stem cell gene therapy:assessing the relevance of preclinical models Nucleic acid therapy for lifespan prolongation: present and future Retroviral integrations in gene therapy trials Hematopoietic stem cell engineering at a crossroads Advances in understanding and treating dystrophic epidermolysis bullosa Gene therapy on the move Neural stem cells could serve as a therapeutic material for age-related neurodegenerative diseases Advances in unrelated and alternative donor hematopoietic cell transplantation for nonmalignant disorders Is genetic rescue of cystinosis an achievable treatment goal?Current translational and clinical practices in hematopoietic cell and gene therapy Allele-specific silencing of mutant huntingtin in rodent brain and human stem cells ABC Transporter Subfamily D: Distinct Differences in Behavior between ABCD1-3 and ABCD4 in Subcellular Localization, Function, and Human Disease Genetically modified mesenchymal stromal cells in cancer therapy Retroviral vectors and transposons for stable gene therapy: advances, current challenges and perspectives Identifying Cancer Driver Genes Using Replication-Incompetent Retroviral Vectors Manufacture of tumor- and virus-specific T lymphocytes for adoptive cell therapies In vivo genome editing restores haemostasis in a mouse model of haemophilia

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Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy.

http://www.wikidata.org/entity/Q35011497

description

2009 nî lūn-bûn

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2009 թուականի Նոյեմբերին հրատարակուած գիտական յօդուած

@hyw

2009 թվականի նոյեմբերին հրատարակված գիտական հոդված

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2009年の論文

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2009年論文

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2009年論文

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2009年論文

@zh-hk

2009年論文

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2009年論文

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2009年论文

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name

Hematopoietic stem cell gene t ...... X-linked adrenoleukodystrophy.

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Hematopoietic stem cell gene t ...... X-linked adrenoleukodystrophy.

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type

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Hematopoietic stem cell gene t ...... X-linked adrenoleukodystrophy.

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Hematopoietic stem cell gene t ...... X-linked adrenoleukodystrophy.

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prefLabel

Hematopoietic stem cell gene t ...... X-linked adrenoleukodystrophy.

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Hematopoietic stem cell gene t ...... X-linked adrenoleukodystrophy.

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SCIENCE.1171242

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Hematopoietic stem cell gene t ...... X-linked adrenoleukodystrophy.

@en

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Bruno l'Homme

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Cynthia C Bartholomae

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Céline Bellesme

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Denice Mittelstaedt

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François Lefrère

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Gabor Veres

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Ina Kutschera

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Liliane Dal-Cortivo

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Manfred Schmidt

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Michel Vidaud

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10.1126/SCIENCE.1171242

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Marina Cavazzana-Calvo

Veronique Kiermer

Salima Hacein-Bey-Abina

Laure Caccavelli

Christof Von Kalle

Philippe Leboulch

Pierre Bougnères

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2009-11-01T00:00:00Z

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38070466

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