about
Transfusion independence and HMGA2 activation after gene therapy of human β-thalassaemiaCurrent and future alternative therapies for beta-thalassemia majorPreclinical evaluation of efficacy and safety of an improved lentiviral vector for the treatment of β-thalassemia and sickle cell disease.Arrayed lentiviral barcoding for quantification analysis of hematopoietic dynamics.Comparative HMG-box sequences of the SRY gene between sheep, cattle and goatsIs normal hematopoiesis maintained solely by long-term multipotent stem cells?Hematopoietic stem cell gene therapy with a lentiviral vector in X-linked adrenoleukodystrophy.Correction of murine β-thalassemia after minimal lentiviral gene transfer and homeostatic in vivo erythroid expansion.Distribution of lentiviral vector integration sites in mice following therapeutic gene transfer to treat β-thalassemia.An activin receptor IIA ligand trap corrects ineffective erythropoiesis in β-thalassemia.Highly efficient in vitro and in vivo delivery of functional RNAs using new versatile MS2-chimeric retrovirus-like particles.Gene Therapy of the β-Hemoglobinopathies by Lentiviral Transfer of the β(A(T87Q))-Globin Gene.Characterization of ovine SRY transcript and developmental expression of genes involved in sexual differentiation.The ovine SOX2 gene: sequence, chromosomal localization and gonadal expression.High-Efficiency Transduction of Primary Human Hematopoietic Stem/Progenitor Cells by AAV6 Vectors: Strategies for Overcoming Donor-Variation and Implications in Genome Editing.Advances in stem cell transplantation and gene therapy in the β-hemoglobinopathies.Sheep gene mapping: assignment of ALDOB, CYP19, WT and SOX2 by somatic cell hybrid analysis.Gene Therapy in a Patient with Sickle Cell Disease.Nucleotide sequence of XLPOU3 cDNA, a member of the POU domain gene family expressed in Xenopus laevis embryos.Control of sex determination in animals.Long-term doxycycline-regulated secretion of erythropoietin by encapsulated myoblasts.Transplantation of Macaca cynomolgus iPS-derived hematopoietic cells in NSG immunodeficient mice.Parallel assessment of globin lentiviral transfer in induced pluripotent stem cells and adult hematopoietic stem cells derived from the same transplanted β-thalassemia patient.Ex Vivo Selection of Transduced Hematopoietic Stem Cells for Gene Therapy of β-Hemoglobinopathies.Lentivirus vectors in β-thalassemia.Evolutionary conservation of a microsatellite in the Wilms tumour (WT) gene: mapping in sheep and cattle.Gene Therapy in Patients with Transfusion-Dependent β-ThalassemiaProtective effects of phosphodiesterase-4 (PDE-4) inhibition in the early phase of pulmonary arterial hypertension in transgenic sickle cell miceHemoglobin disorders: lentiviral gene therapy in the starting blocks to enter clinical practiceImprovement of mouse beta-thalassemia by electrotransfer of erythropoietin cDNA.Sequence evolution of SRY gene within Bovidae family[The genetics of sex]Enhanced Transduction of Macaca fascicularis Hematopoietic Cells with Chimeric Lentiviral Vectors
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description
researcher
@en
wetenschapper
@nl
հետազոտող
@hy
name
Emmanuel Payen
@ast
Emmanuel Payen
@en
Emmanuel Payen
@es
Emmanuel Payen
@nl
type
label
Emmanuel Payen
@ast
Emmanuel Payen
@en
Emmanuel Payen
@es
Emmanuel Payen
@nl
prefLabel
Emmanuel Payen
@ast
Emmanuel Payen
@en
Emmanuel Payen
@es
Emmanuel Payen
@nl
P106
P31
P496
0000-0002-1329-2327